Adults with Duchenne muscular dystrophy demonstrated functional improvements exceeding natural history, following 28-day treatment with SAT-3247Grip strength increased 118.6% and predicted forced ...
"In many countries, health insurance changes when DMD men are no longer seen in a specialized pediatric center. This impacts massively on the quality of care they receive. For this reason, many DMD ...
Data from first cohort of five participants suggest an acceptable safety profile for AB-1003 in participants with limb-girdle ...
Satellos Bioscience (MSCLF) announced new data further demonstrating tolerability and initial efficacy of SAT-3247 in adults with Duchenne ...
Satellos Bioscience ( (TSE:MSCL) ) has issued an update. Satellos Bioscience announced promising new data from a Phase 1a/b trial of SAT-3247, a potential treatment for Duchenne muscular dystrophy ...
Editor’s note: This is an automatically generated transcript. Please notify [email protected] if there are concerns regarding accuracy of the transcription. Patient advocacy organizations often bring ...
Edgewise Therapeutics Inc EWTX released 12-month topline results from the ARCH study, an open-label, single-center study assessing EDG-5506 in adults with Becker Muscular Dystrophy (BMD). EDG-5506 is ...
PepGen’s stock has risen by more than 120% after its investigational myotonic dystrophy type 1 (DM1) candidate reported the highest mean splicing correction in a Phase I trial. In the FREEDOM-DM1 ...
ST. LOUIS — On a beautiful day in Forest Park, dozens of people brought hope to kids and adults with Muscular Dystrophy by just taking a long walk. The Muscular Dystrophy Association used the walk to ...
Company now has three distinct rare disease programs in clinical development - myotonic dystrophy type 1 (DM1), facioscapulohumeral muscular dystrophy (FSHD), and Duchenne muscular dystrophy (DMD) ...
The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...