1st Michigan patient undergoes FDA-authorized sickle cell gene therapy

Chantez Sanford Jr., 24, of Southfield, says his life has been transformed after undergoing Lyfgenia gene therapy at Children ...
Afro

Addressing sickle cell disease: The importance of genetic counseling

People are often encouraged to “know their status,” however this healthy habit can be applied to more than just safe-sex practices. Although they are not the only community who suffers with sickle ...
Afro

Unlocking sickle cell mysteries: Dr. Ambroise Wonkam speaks on genetic modifiers and patient outcomes

When Dr. Ambroise Wonkam walked into a panel on medical genetics out of curiosity, he had no idea it would shape the course of his career. Born in Cameroon, Wonkam has dedicated his career to studying ...
News Medical

First U.S. trial uses non-viral CRISPR to correct sickle cell mutation

UCSF Benioff Children's Hospital Oakland is enrolling patients in an innovative clinical trial that seeks to cure sickle cell disease. The trial is the first in the U.S. to apply non-viral CRISPR-Cas9 ...
The Boston Globe

Vertex’s CRISPR treatment for sickle cell disease hits unexpected roadblock

This story is republished from STAT, the health and medicine news site that’s a partner to the Globe. Sign up for STAT’s free Morning Rounds newsletter here. Vertex executives warned that Casgevy, its ...
Labroots

Sickle Cell Patient is Successfully Treated with a Novel Gene Therapy

Sickle cell disease refers to a group of genetic diseases that impact a protein that ferries oxygen through the blood. That protein is called hemoglobin, and in sickle cell disease, aberrant ...
The Conversation

Sickle cell disease is a genetic disorder that causes lifelong suffering – here’s what you need to know

Cristina Pina receives funding from Children's Cancer and Leukaemia Group via the Little Princess Trust and the National Centre for the Replacement, Reduction and Refinement of Animals in Research.
Hosted on MSN

‘Much-needed hope’ as CRISPR gene editing therapy recommended for sickle cell disease

Some with severe sickle cell disease in England will now be able to access landmark CRISPR gene editing therapy, according to new health guidelines which were hailed as marking a “significant shift” ...